A Micro-RNA Approach for the Treatment of Spinocerebellar Ataxia Type 6 (SCA6)
SUMMARY Spinocerebellar ataxia type 6 (SCA6) is a rare, dominantly inherited disease that causes Purkinje cell degradation and results in: loss of coordination, tremors, and uncoordinated muscle movement. Current therapies only mitigate symptoms and do not address the underlying pathophysiology responsible for disease progression. It is known that individuals with… Read More